Development of the SIOPE DIPG network, registry and imaging repository: a collaborative effort to optimize research into a rare and lethal disease


Por: van Zanten SE, Baugh J, Chaney B, De Jongh D, Aliaga ES, Barkhof F, Noltes J, De Wolf R, Van Dijk J, Cannarozzo A, Damen-Korbijn CM, Lieverst JA, Colditz N, Hoffmann M, Warmuth-Metz M, Bison B, Jones DT, Sturm D, Gielen GH, Jones C, Hulleman E, Calmon R, Castel D, Varlet P, Giraud G, Slavc I, Van Gool S, Jacobs S, Jadrijevic-Cvrlje F, Sumerauer D, Nysom K, Pentikainen V, Kivivuori SM, Leblond P, Entz-Werle N, von Bueren AO, Kattamis A, Hargrave DR, Hauser P, Garami M, Thorarinsdottir HK, Pears J, Gandola L, Rutkauskiene G, Janssens GO, Torsvik IK, Perek-Polnik M, Gil-da-Costa MJ, Zheludkova O, Shats L, Deak L, Kitanovski L, Cruz-Martínez O, Morales-La Madrid A, Holm S, Gerber N, Kebudi R, Grundy R, Lopez-Aguilar E, Zapata-Tarres M, Emmerik J, Hayden T, Bailey S, Biassoni V, Massimino M, Grill J, Vandertop WP, Kaspers GJ, Fouladi M, Kramm CM, van Vuurden DG and members of the SIOPE DIPG Network

Publicada: 1 abr 2017 Ahead of Print: 21 ene 2017
Resumen:
Diffuse intrinsic pontine glioma (DIPG) is a rare and deadly childhood malignancy. After 40 years of mostly single-center, often non-randomized trials with variable patient inclusions, there has been no improvement in survival. It is therefore time for international collaboration in DIPG research, to provide new hope for children, parents and medical professionals fighting DIPG. In a first step towards collaboration, in 2011, a network of biologists and clinicians working in the field of DIPG was established within the European Society for Paediatric Oncology (SIOPE) Brain Tumour Group: the SIOPE DIPG Network. By bringing together biomedical professionals and parents as patient representatives, several collaborative DIPG-related projects have been realized. With help from experts in the fields of information technology, and legal advisors, an international, web-based comprehensive database was developed, The SIOPE DIPG Registry and Imaging Repository, to centrally collect data of DIPG patients. As for April 2016, clinical data as well as MR-scans of 694 patients have been entered into the SIOPE DIPG Registry/Imaging Repository. The median progression free survival is 6.0 months (95% Confidence Interval (CI) 5.6-6.4 months) and the median overall survival is 11.0 months (95% CI 10.5-11.5 months). At two and five years post-diagnosis, 10 and 2% of patients are alive, respectively. The establishment of the SIOPE DIPG Network and SIOPE DIPG Registry means a paradigm shift towards collaborative research into DIPG. This is seen as an essential first step towards understanding the disease, improving care and (ultimately) cure for children with DIPG.

Filiaciones:
van Zanten SE:
 Department of Paediatrics, Division of Oncology/Haematology, VU University Medical Center, Amsterdam, The Netherlands.

Baugh J:
 Department of Pediatrics, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, USA

Chaney B:
 Department of Pediatrics, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, USA

De Jongh D:
 2TCI B.V., Breda, The Netherlands

Aliaga ES:
 Department of Radiology and Nuclear Medicine, VU University Medical Center, Amsterdam, The Netherlands

Barkhof F:
 Department of Radiology and Nuclear Medicine, VU University Medical Center, Amsterdam, The Netherlands

 Institutes of Neurology and Healthcare Engineering, UCL, London, UK

Noltes J:
 KPMG, Amstelveen, The Netherlands

De Wolf R:
 KPMG, Amstelveen, The Netherlands

Van Dijk J:
 Yellow Research B.V., Amsterdam, The Netherlands

Cannarozzo A:
 Trasferimento Tecnologico (TTO), Fondazione IRCCS Istituto Nazionale dei Tumori, Milano, Italy

Damen-Korbijn CM:
 Dutch Childhood Oncology Group (DCOG), The Hague, The Netherlands

Lieverst JA:
 Dutch Childhood Oncology Group (DCOG), The Hague, The Netherlands

Colditz N:
 Division of Pediatric Hematology and Oncology, Department of Child and Adolescent Health, University of Göttingen, Göttingen, Germany

Hoffmann M:
 Division of Pediatric Hematology and Oncology, Department of Child and Adolescent Health, University of Göttingen, Göttingen, Germany

Warmuth-Metz M:
 Division of Pediatric Neurooncology, German Cancer Research Center (DKFZ) Heidelberg, Heidelberg, Germany

Bison B:
 Division of Pediatric Neurooncology, German Cancer Research Center (DKFZ) Heidelberg, Heidelberg, Germany

Jones DT:
 Institute of Neuropathology, University of Bonn Medical Center, Bonn, Germany

Sturm D:
 Institute of Neuropathology, University of Bonn Medical Center, Bonn, Germany

Gielen GH:
 Institute of Neuropathology, University of Bonn Medical Center, Bonn, Germany

Jones C:
 Divisions of Molecular Pathology and Cancer Therapeutics, The Institute of Cancer Research, Sutton, UK

Hulleman E:
 Neuro-oncology Research Group, VU University Medical Center, Amsterdam, The Netherlands

Calmon R:
 Université Paris-Descartes, Hôpital Necker-Enfants malades, Paris, France

Castel D:
 UMR 8203 CNRS, Gustave Roussy, Paris-Saclay University, Villejuif, France

Varlet P:
 Service de Neuropathologie, Hôpital Sainte-Anne, Paris, France

Giraud G:
 Institut Gustave Roussy, Villejuif, France

Slavc I:
 Department of Pediatrics and Adolescent Medicine, Medical University of Vienna, Vienna, Austria

Van Gool S:
 Immuno-oncology Centre Köln, Cologne, Germany

Jacobs S:
 Department of Pediatric Hematology and Oncology, University Hospitals Leuven, Leuven, Belgium

 Department of Microbiology and Immunology, KU Leuven, Leuven, Belgium

Jadrijevic-Cvrlje F:
 Department of Oncology and Hematology, Children's Hospital Zagreb, Zagreb, Croatia

Sumerauer D:
 Department of Pediatric Hematology and Oncology, 2nd Faculty of Medicine, University Hospital Motol, Charles University, Prague, Czech Republic

Nysom K:
 Pediatrics and Adolescent Medicine, University Hospital Rigshospitalet, Copenhagen, Denmark

Pentikainen V:
 Division of Hematology-Oncology and Stem Cell Transplantation, Children's Hospital, Helsinki University Hospital, Helsinki, Finland

Kivivuori SM:
 Helsinki University Hospital (HUH) and HUH Children and Adolescents, Helsinki, Finland

Leblond P:
 Pediatric Oncology Unit, Oscar Lambret Comprehensive Cancer Center, Lille, France

Entz-Werle N:
 Service de Pédiatrie Onco-Hématologie, CHRU Hautepierre Strasbourg, Strasbourg, France

von Bueren AO:
 Pediatric Oncology and Hematology, Department of Pediatrics, University Hospital of Geneva, Genève, Switzerland

Kattamis A:
 First Department of Pediatrics, National and Kapodistrian University of Athens, 'Aghia Sofia' Children's Hospital, Athens, Greece

Hargrave DR:
 Paediatric Oncology Unit, Great Ormond Street Hospital (GOSH), London, UK

Hauser P:
 Second Department of Pediatrics, Semmelweis University, Budapest, Hungary

Garami M:
 Second Department of Pediatrics, Semmelweis University, Budapest, Hungary

Thorarinsdottir HK:
 Pediatric Hematology-Oncology, The Children's Hospital, Reykjavik, Iceland

Pears J:
 Department of Paediatric Oncology, Our Lady's Children's Hospital, Crumlin, Dublin, Ireland

Gandola L:
 Pediatric Radiotherapy Unit, Department of Diagnostic Radiology and Radiotherapy, Fondazione IRCCS Istituto Nazionale dei Tumori, Milano, Italy

Rutkauskiene G:
 Department of Pediatric Oncology and Hematology, Hospital of Lithuanian University of Health Sciences Kaunas Clinic, Kaunas, Lithuania

Janssens GO:
 Department of Radiation Oncology, University Medical Center Utrecht and Princess Maxima Center for Pediatric Oncology, Utrecht, The Netherlands

Torsvik IK:
 Department of Pediatrics, Division of Oncology/Hematology, Haukeland University Hospital, Mons, Norway

Perek-Polnik M:
 Department of Oncology, The Children's Memorial Health Institute, Warsaw, Poland

Gil-da-Costa MJ:
 Pediatric Hemathology and Oncology Division, University Hospital S. João Alameda Hernani Monteiro, Porto, Portugal

Zheludkova O:
 Department of Neuro-Oncology, Russian Scientific Center of Radiology, Moscow, Russia

Shats L:
 Department of Children Oncology and Haematology, City Clinical Hospital #31 of Saint-Petersburg, St.-Petersburg, Russian Federation

Deak L:
 Department of Pediatric Oncology/ Haematology, Children University Hospital, Kosice, Slovakia

Kitanovski L:
 Department of Pediatrics, Division of Haematooncology, University Medical Center Ljubljana, Ljubljana, Slovenia

Cruz-Martínez O:
 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Déu, Barcelona, Spain

Morales-La Madrid A:
 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Déu, Barcelona, Spain

Holm S:
 Department of Pediatric Hematology and Oncology, Department of Woman and Child Health, Karolinska University Hospital, Stockholm, Sweden

Gerber N:
 Department of Oncology, University Children's Hospital of Zurich, Zurich, Switzerland

Kebudi R:
 Cerrahpasa Medical Faculty & Oncology Institute, Pediatric Hematology-Oncology, Istanbul University, Istanbul, Turkey

Grundy R:
 Children's Brain Tumour Research Centre, The Medical School, University of Nottingham, Nottingham, UK

Lopez-Aguilar E:
 Jefatura de Servicio de Oncología, Hospital de Pediatría, Centro Médico Nacional Siglo XXI, Instituto Mexicano del Seguro Social, Distrito Federal, Mexico

Zapata-Tarres M:
 Division of Pediatric Oncology, Hospital Infantil de Mexico Federico Gomez, Mexico City, Mexico

Emmerik J:
 Stichting Semmy, Weesp, The Netherlands

Hayden T:
 The DIPG Collaborative, Cincinnati, USA

Bailey S:
 Great North Childrens Hospital, Victoria Wing, Royal Victoria Infirmary, Newcastle upon Tyne, UK

Biassoni V:
 Pediatric Oncology Unit, Fondazione IRCCS Istituto Nazionale dei Tumori, Milano, Italy

Massimino M:
 Pediatric Oncology Unit, Fondazione IRCCS Istituto Nazionale dei Tumori, Milano, Italy

Grill J:
 Institut Gustave Roussy, Villejuif, France

Vandertop WP:
 Neurosurgical Center Amsterdam, Academic Medical Center and VU University Medical Center, Amsterdam, The Netherlands

Kaspers GJ:
 Department of Paediatrics, Division of Oncology/Haematology, VU University Medical Center, Amsterdam, The Netherlands

 Academy of Princess Máxima Center for Pediatric Oncology, Lundlaan 6, 3584 EA, Utrecht, The Netherlands

Fouladi M:
 Department of Pediatrics, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, USA

Kramm CM:
 Division of Pediatric Hematology and Oncology, Department of Child and Adolescent Health, University of Göttingen, Göttingen, Germany

van Vuurden DG:
 Department of Paediatrics, Division of Oncology/Haematology, VU University Medical Center, Amsterdam, The Netherlands
ISSN: 0167594X





JOURNAL OF NEURO-ONCOLOGY
Editorial
SPRINGER, ONE NEW YORK PLAZA, SUITE 4600 , NEW YORK, NY 10004, UNITED STATES, Países Bajos
Tipo de documento: Article
Volumen: 132 Número: 2
Páginas: 255-266
WOS Id: 000399015500007
ID de PubMed: 28110411
imagen Green Submitted, Green Published, hybrid

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