Targeted drug distribution in tumor extracellular fluid of GD2-expressing neuroblastoma patient-derived xenografts using SN-38-loaded nanoparticles conjugated to the monoclonal antibody 3F8


Por: Monterrubio C, Paco-Mercader S, Gene-Olaciregui N, Pascual-Pastó G, Vilà-Ubach M, Cuadrado-Vilanova M, Ferrandiz MM, Castillo-Ecija H, Glisoni R, Kuplennik N, Jungbluth A, de Torres C, Lavarino C, Cheung NV, Mora J, Sosnik A and Carcaboso AM

Publicada: 10 ene 2017 Ahead of Print: 12 abr 2017
Categoría: Pharmaceutical science

Resumen:
Neuroblastoma is a pediatric solid tumor with high expression of the tumor associated antigen disialoganglioside GD2. Despite initial response to induction therapy, nearly 50% of high-risk neuroblastomas recur because of chemoresistance. Here we encapsulated the topoisomerase-I inhibitor SN-38 in polymeric nanoparticles (NPs) surface-decorated with the anti-GD2 mouse mAb 3F8 at a mean density of seven antibody molecules per NP. The accumulation of drug-loaded NPs targeted with 3F8 versus with control antibody was monitored by microdialysis in patient-derived GD2-expressing neuroblastoma xenografts. We showed that the extent of tumor penetration by SN-38 was significantly higher in mice receiving the targeted nano-drug delivery system when compared to non-targeted system or free drug. This selective penetration of the tumor extracellular fluid translated into a strong anti-tumor effect prolonging survival of mice bearing GD2-high neuroblastomas in vivo.

Filiaciones:
Monterrubio C:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Paco-Mercader S:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Pascual-Pastó G:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Vilà-Ubach M:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Cuadrado-Vilanova M:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Ferrandiz MM:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Castillo-Ecija H:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Glisoni R:
 CONICET-Department of Pharmaceutical Technology, Faculty of Pharmacy and Biochemistry, Universidad de Buenos Aires, CP1113 Buenos Aires, Argentina

Kuplennik N:
 Laboratory of Pharmaceutical Nanomaterials Science, Department of Materials Science and Engineering, Technion-Israel Institute of Technology, 3200003 Haifa, Israel

Jungbluth A:
 Memorial Sloan-Kettering Cancer Center, New York, NY 10021, USA

de Torres C:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Lavarino C:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Cheung NV:
 Memorial Sloan-Kettering Cancer Center, New York, NY 10021, USA

Mora J:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain

Sosnik A:
 Laboratory of Pharmaceutical Nanomaterials Science, Department of Materials Science and Engineering, Technion-Israel Institute of Technology, 3200003 Haifa, Israel

Carcaboso AM:
 Institut de Recerca Sant Joan de Déu, 08950 Barcelona, Spain

 Department of Pediatric Hematology and Oncology, Hospital Sant Joan de Deu, 08950 Barcelona, Spain.
ISSN: 01683659





JOURNAL OF CONTROLLED RELEASE
Editorial
ELSEVIER, RADARWEG 29, 1043 NX AMSTERDAM, NETHERLANDS, Países Bajos
Tipo de documento: Article
Volumen: 255 Número:
Páginas: 108-119
WOS Id: 000402428900011
ID de PubMed: 28412222
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