Histamine signaling and metabolism identify potential biomarkers and therapies for lymphangioleiomyomatosis.


Por: Herranz C, Mateo F, Baiges A, Ruiz de Garibay G, Junza A, Johnson SR, Miller S, García N, Capellades J, Gómez A, Vidal A, Palomero L, Espín R, Extremera AI, Blommaert E, Revilla-López E, Saez B, Gómez-Ollés S, Ancochea J, Valenzuela C, Alonso T, Ussetti P, Laporta R, Xaubet A, Rodríguez-Portal JA, Montes-Worboys A, Machahua C, Bordas J, Menendez JA, Cruzado JM, Guiteras R, Bontoux C, La Motta C, Noguera-Castells A, Mancino M, Lastra E, Rigo-Bonnin R, Perales JC, Viñals F, Lahiguera A, Zhang X, Cuadras-Palleja D, van Moorsel CHM, van der Vis JJ, Quanjel MJR, Filippakis H, Hakem R, Gorrini C, Ferrer M, Ugun-Klusek A, Billett E, Radzikowska E, Casanova Á, Molina-Molina M, Roman A, Yanes O and Pujana MA

Publicada: 7 sep 2021 Ahead of Print: 11 ago 2021
Categoría: Molecular medicine

Resumen:
Inhibition of mTOR is the standard of care for lymphangioleiomyomatosis (LAM). However, this therapy has variable tolerability and some patients show progressive decline of lung function despite treatment. LAM diagnosis and monitoring can also be challenging due to the heterogeneity of symptoms and insufficiency of non-invasive tests. Here, we propose monoamine-derived biomarkers that provide preclinical evidence for novel therapeutic approaches. The major histamine-derived metabolite methylimidazoleacetic acid (MIAA) is relatively more abundant in LAM plasma, and MIAA values are independent of VEGF-D. Higher levels of histamine are associated with poorer lung function and greater disease burden. Molecular and cellular analyses, and metabolic profiling confirmed active histamine signaling and metabolism. LAM tumorigenesis is reduced using approved drugs targeting monoamine oxidases A/B (clorgyline and rasagiline) or histamine H1 receptor (loratadine), and loratadine synergizes with rapamycin. Depletion of Maoa or Hrh1 expression, and administration of an L-histidine analog, or a low L-histidine diet, also reduce LAM tumorigenesis. These findings extend our knowledge of LAM biology and suggest possible ways of improving disease management.

Filiaciones:
Herranz C:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Mateo F:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Baiges A:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Ruiz de Garibay G:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Junza A:
 Department of Electronic Engineering, Institute of Health Research Pere Virgili (IIPSV), University Rovira i Virgili, Tarragona, Spain

 Biomedical Research Network Centre in Diabetes and Associated Metabolic Diseases (CIBERDEM), Instituto de Salud Carlos III, Madrid, Spain

Johnson SR:
 National Centre for Lymphangioleiomyomatosis, Nottingham University Hospitals NHS Trust, Nottinghamshire, Division of Respiratory Medicine, University of Nottingham, Nottingham, UK

Miller S:
 National Centre for Lymphangioleiomyomatosis, Nottingham University Hospitals NHS Trust, Nottinghamshire, Division of Respiratory Medicine, University of Nottingham, Nottingham, UK

García N:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Capellades J:
 Department of Electronic Engineering, Institute of Health Research Pere Virgili (IIPSV), University Rovira i Virgili, Tarragona, Spain

 Biomedical Research Network Centre in Diabetes and Associated Metabolic Diseases (CIBERDEM), Instituto de Salud Carlos III, Madrid, Spain

Gómez A:
 Centre for Genomic Regulation, Barcelona Institute of Science and Technology, Barcelona, Spain

Vidal A:
 Department of Pathology, University Hospital of Bellvitge, Oncobell, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

 CIBER on Cancer (CIBERONC), Instituto de Salud Carlos III, Madrid, Spain

Palomero L:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Espín R:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Extremera AI:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Blommaert E:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Revilla-López E:
 Lung Transplant Unit, Pneumology Service, Lymphangioleiomyomatosis Clinic, Vall d'Hebron University Hospital, Barcelona, Spain

Saez B:
 Lung Transplant Unit, Pneumology Service, Lymphangioleiomyomatosis Clinic, Vall d'Hebron University Hospital, Barcelona, Spain

Gómez-Ollés S:
 Lung Transplant Unit, Pneumology Service, Lymphangioleiomyomatosis Clinic, Vall d'Hebron University Hospital, Barcelona, Spain

Ancochea J:
 Pneumology Service, La Princesa Research Institute, University Hospital La Princesa, Madrid, Spain

Valenzuela C:
 Pneumology Service, La Princesa Research Institute, University Hospital La Princesa, Madrid, Spain

Alonso T:
 Pneumology Service, La Princesa Research Institute, University Hospital La Princesa, Madrid, Spain

Ussetti P:
 Pneumology Service, University Hospital Clínica Puerta del Hierro, Majadahonda, Madrid, Spain

Laporta R:
 Pneumology Service, University Hospital Clínica Puerta del Hierro, Majadahonda, Madrid, Spain

Xaubet A:
 Pneumology Service, Hospital Clínic de Barcelona, Barcelona, Spain

Rodríguez-Portal JA:
 Medical-Surgical Unit of Respiratory Diseases, Institute of Biomedicine of Seville (IBiS), University Hospital Virgen del Rocío, Seville, Spain

 Biomedical Research Network Centre in Respiratory Diseases (CIBERES), Instituto de Salud Carlos III, Madrid, Spain

Montes-Worboys A:
 Biomedical Research Network Centre in Respiratory Diseases (CIBERES), Instituto de Salud Carlos III, Madrid, Spain

 Interstitial Lung Disease Unit, Department of Respiratory Medicine, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Machahua C:
 Biomedical Research Network Centre in Respiratory Diseases (CIBERES), Instituto de Salud Carlos III, Madrid, Spain

 Interstitial Lung Disease Unit, Department of Respiratory Medicine, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Bordas J:
 Biomedical Research Network Centre in Respiratory Diseases (CIBERES), Instituto de Salud Carlos III, Madrid, Spain

 Interstitial Lung Disease Unit, Department of Respiratory Medicine, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Menendez JA:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Cruzado JM:
 Experimental Nephrology, Department of Clinical Sciences, University of Barcelona, Barcelona, Spain

 Department of Nephrology, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Guiteras R:
 Experimental Nephrology, Department of Clinical Sciences, University of Barcelona, Barcelona, Spain

 Department of Nephrology, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Bontoux C:
 Department of Pathology, University Hospital Pitié-Salpêtrière, Faculty of Medicine, University of Sorbonne, Paris, France

La Motta C:
 Department of Pharmacy, University of Pisa, Pisa, Italy

Noguera-Castells A:
 Biomedical Research Institute "August Pi i Sunyer" (IDIBAPS), Department of Medicine, University of Barcelona, Barcelona, Spain

Mancino M:
 Biomedical Research Institute "August Pi i Sunyer" (IDIBAPS), Department of Medicine, University of Barcelona, Barcelona, Spain

Lastra E:
 Genetic Counseling Unit, Department of Medical Oncology, University Hospital of Burgos, Burgos, Spain

Rigo-Bonnin R:
 Clinical Laboratory, University Hospital of Bellvitge, IDIBELL, L'Hospitalet de Llobregat, Barcelona, Spain

Perales JC:
 Department of Physiological Science II, University of Barcelona, Barcelona, Spain

Viñals F:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

 Department of Physiological Science II, University of Barcelona, Barcelona, Spain

Lahiguera A:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain

Zhang X:
 National Center for Advancing Translational Sciences (NCATS), National Institute of Health (NIH), Bethesda, MD, USA

Cuadras-Palleja D:
 Statistics Department, Foundation Sant Joan de Déu, Esplugues, Spain

van Moorsel CHM:
 Interstitial Lung Disease (ILD) Center of Excellence, St. Antonius Hospital, Nieuwegein, The Netherlands

van der Vis JJ:
 Interstitial Lung Disease (ILD) Center of Excellence, St. Antonius Hospital, Nieuwegein, The Netherlands

Quanjel MJR:
 Interstitial Lung Disease (ILD) Center of Excellence, St. Antonius Hospital, Nieuwegein, The Netherlands

Filippakis H:
 Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA, USA

Hakem R:
 Princess Margaret Cancer Centre, University Health Network, Department of Medical Biophysics, University of Toronto, Toronto, Ontario, Canada

Gorrini C:
 Princess Margaret Hospital, The Campbell Family Institute for Breast Cancer Research, Ontario Cancer Institute, University Health Network, Toronto, ON, Canada

Ferrer M:
 National Center for Advancing Translational Sciences (NCATS), National Institute of Health (NIH), Bethesda, MD, USA

Ugun-Klusek A:
 Centre for Health, Ageing and Understanding Disease (CHAUD), School of Science and Technology, Nottingham Trent University, Nottingham, UK

Billett E:
 Centre for Health, Ageing and Understanding Disease (CHAUD), School of Science and Technology, Nottingham Trent University, Nottingham, UK

Radzikowska E:
 Department of Lung Diseases III, National Tuberculosis and Lung Disease Research Institute, Warsaw, Poland

Casanova Á:
 Pneumology Service, University Hospital of Henares, University Francisco de Vitoria, Coslada, Madrid, Spain

Molina-Molina M:
 Biomedical Research Network Centre in Respiratory Diseases (CIBERES), Instituto de Salud Carlos III, Madrid, Spain

 Interstitial Lung Disease Unit, Department of Respiratory Medicine, University Hospital of Bellvitge, IDIBELL, L'Hospitalet del Llobregat, Barcelona, Spain

Roman A:
 Lung Transplant Unit, Pneumology Service, Lymphangioleiomyomatosis Clinic, Vall d'Hebron University Hospital, Barcelona, Spain

Yanes O:
 Department of Electronic Engineering, Institute of Health Research Pere Virgili (IIPSV), University Rovira i Virgili, Tarragona, Spain

 Biomedical Research Network Centre in Diabetes and Associated Metabolic Diseases (CIBERDEM), Instituto de Salud Carlos III, Madrid, Spain

Pujana MA:
 ProCURE, Catalan Institute of Oncology, Oncobell, Bellvitge Institute for Biomedical Research (IDIBELL), L'Hospitalet del Llobregat, Barcelona, Spain
ISSN: 17574676





EMBO Molecular Medicine
Editorial
SPRINGERNATURE, CAMPUS, 4 CRINAN ST, LONDON N1 9XW, ENGLAND, Estados Unidos America
Tipo de documento: Article
Volumen: 13 Número: 9
Páginas:
WOS Id: 000683691400001
ID de PubMed: 34378323
imagen Green Published

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