The antitumour drug ABTL0812 impairs neuroblastoma growth through endoplasmic reticulum stress-mediated autophagy and apoptosis


Por: París-Coderch, L, Soriano, A, Jiménez, C, Erazo, T, Muñoz-Guardiola, P, Masanas, M, Antonelli, R, Boloix, A, Alfón, J, Pérez-Montoyo, H, Yeste-Velasco, M, Domènech, C, Roma, J, Sanchez deToledo J, Moreno, L, Lizcano, JM, Gallego, S and Segura, MF

Publicada: 17 sep 2020
Resumen:
Neuroblastoma is the leading cause of cancer death in children aged 1 to 4 years. Particularly, five-year overall survival for high-risk neuroblastoma is below 50% with no curative options when refractory or relapsed. Most of current therapies target cell division and proliferation, thereby inducing DNA damage and programmed cell death. However, aggressive tumours often present alterations of these processes and are resistant to therapy. Therefore, exploring alternative pathways to induce tumour cell death will provide new therapeutic opportunities for these patients. In this study we aimed at testing the therapeutic potential of ABTL0812, a novel anticancer drug that induces cytotoxic autophagy to eliminate cancer cells, which is currently in phase II clinical trials of adult tumours. Here, we show that ABTL0812 impaired the viability of clinical representative neuroblastoma cell lines regardless of genetic alterations associated to bad prognosis and resistance to therapy. Oral administration of ABTL0812 to mice bearing neuroblastoma xenografts impaired tumour growth. Furthermore, our findings revealed that, in neuroblastoma, ABTL0812 induced cancer cell death via induction of endoplasmic reticulum stress, activation of the unfolded protein response, autophagy and apoptosis. Remarkably, ABTL0812 potentiated the antitumour activity of chemotherapies and differentiating agents such as irinotecan and 13-cis-retinoic acid. In conclusion, ABTL0812 distinctive mechanism of action makes it standout to be used alone or in combination in high-risk neuroblastoma patients.

Filiaciones:
París-Coderch, L:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Soriano, A:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Jiménez, C:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Erazo, T:
 Univ Autonoma Barcelona, Prot Kinases & Signal Transduct Lab, Inst Neurociencies, Bellaterra, Spain

 Univ Autonoma Barcelona, Dept Bioquim & Biol Mol, Bellaterra, Spain

Muñoz-Guardiola, P:
 Univ Autonoma Barcelona, Prot Kinases & Signal Transduct Lab, Inst Neurociencies, Bellaterra, Spain

 Univ Autonoma Barcelona, Dept Bioquim & Biol Mol, Bellaterra, Spain

 Abil Pharmaceut SL, Avinguda Parc Tecnol 3,Parc Tecnol Valles, Cerdanyola Del Valles, Spain

Masanas, M:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Antonelli, R:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Boloix, A:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Alfón, J:
 Abil Pharmaceut SL, Avinguda Parc Tecnol 3,Parc Tecnol Valles, Cerdanyola Del Valles, Spain

Pérez-Montoyo, H:
 Abil Pharmaceut SL, Avinguda Parc Tecnol 3,Parc Tecnol Valles, Cerdanyola Del Valles, Spain

Yeste-Velasco, M:
 Abil Pharmaceut SL, Avinguda Parc Tecnol 3,Parc Tecnol Valles, Cerdanyola Del Valles, Spain

Domènech, C:
 Abil Pharmaceut SL, Avinguda Parc Tecnol 3,Parc Tecnol Valles, Cerdanyola Del Valles, Spain

Roma, J:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Sanchez deToledo J:
 Univ Autonoma Barcelona, Hosp Univ Vall DHebron, Pediat Oncol & Hematol Unit, Barcelona, Spain

 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

Moreno, L:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

 Univ Autonoma Barcelona, Hosp Univ Vall DHebron, Pediat Oncol & Hematol Unit, Barcelona, Spain

Lizcano, JM:
 Univ Autonoma Barcelona, Prot Kinases & Signal Transduct Lab, Inst Neurociencies, Bellaterra, Spain

 Univ Autonoma Barcelona, Dept Bioquim & Biol Mol, Bellaterra, Spain

Gallego, S:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain

 Univ Autonoma Barcelona, Hosp Univ Vall DHebron, Pediat Oncol & Hematol Unit, Barcelona, Spain

Segura, MF:
 Vall dHebron Inst Recerca VHIR, Translat Res Child & Adolescent Canc, Barcelona, Spain
ISSN: 20414889





Cell Death & Disease
Editorial
SPRINGERNATURE, CAMPUS, 4 CRINAN ST, LONDON N1 9XW, ENGLAND, Reino Unido
Tipo de documento: Article
Volumen: 11 Número: 9
Páginas:
WOS Id: 000574542300009
ID de PubMed: 32943619
imagen gold, Green Published

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