Cysteamine (Cystagon®) adherence in patients with cystinosis in Spain: successful in children and a challenge in adolescents and adults.


Por: Ariceta G, Lara E, Camacho Díaz JA, Oppenheimer F, Vara J, Santos F, Muñoz MA, Cantarell C, Gil Calvo M, Romero R, Valenciano B, García-Nieto V, Sanahuja MJ, Crespo J, Justa ML, Urisarri A, Bedoya R, Bueno A, Daza A, Bravo J, Llamas F and Jiménez Del Cerro LA

Publicada: 1 mar 2015 Ahead of Print: 26 oct 2014
Categoría: Medicine (miscellaneous)

Resumen:
Cysteamine has improved survival and prognosis in cystinosis. Increasing numbers of patients reach adulthood and face new challenges such as compliance that wanes over time. The aim of this study was to evaluate adherence to cysteamine treatment in a group of cystinotic patients in Spain in an attempt to identify potential therapy pitfalls and improve the overall care of affected individuals. Despite the impact of cysteamine on prognosis, there is a paucity of data regarding adherence.

Filiaciones:
Ariceta G:
 Hospital Universitari Vall d' Hebron, Barcelona, Spain Hospital Universitario Cruces, Bilbao, Spain

Lara E:
 Hospital Universitari Vall d' Hebron, Barcelona, Spain

Camacho Díaz JA:
 Hospital Sant Joan de Déu, Barcelona, Spain

Oppenheimer F:
 Hospital Universitari Clínic, Barcelona, Spain

Vara J:
 Hospital Universitario 12 de Octubre, Madrid, Spain

Santos F:
 Hospital Universitario Central de Asturias y Universidad de Oviedo, Oviedo, Spain

Muñoz MA:
 Hospital Universitario Virgen de la Salud, Toledo, Spain

Cantarell C:
 Hospital Universitari Vall d' Hebron, Barcelona, Spain

Gil Calvo M:
 Complexo Hospitalario Universitario de Santiago de Compostela, Santiago de Compostela, Spain

Romero R:
 Complexo Hospitalario Universitario de Santiago de Compostela, Santiago de Compostela, Spain

Valenciano B:
 Hospital Universitario Materno-Infantil Las Palmas, Las Palmas de Gran Canaria, Spain

García-Nieto V:
 Hospital Universitario Ntra. Sra. de la Candelaria, Santa Cruz de Tenerife, Spain

Sanahuja MJ:
 Hospital Universitario La Fe, Valencia, Spain

Crespo J:
 Hospital Universitario Dr Peset, Valencia, Spain

Justa ML:
 Hospital Universitario Miguel Servet, Zaragoza, Spain

Urisarri A:
 Hospital Arquitecto Marcide, Ferrol, Spain

Bedoya R:
 Hospital Universitario Virgen del Rocío, Sevilla, Spain

Bueno A:
 Hospital Universitario Materno-Infantil, Materno-Infantil Carlos Haya, Málaga, Spain

Daza A:
 Complejo Hospitalario de Torrecárdenas, Almería, Spain

Bravo J:
 Hospital Universitario Virgen de las Nieves, Granada, Spain

Llamas F:
 Hospital General de Albacete, Albacete, Spain

Jiménez Del Cerro LA:
 Hospital General Universitario de Alicante, Alicante, Spain
ISSN: 09310509





NEPHROLOGY DIALYSIS TRANSPLANTATION
Editorial
Oxford University Press, England, Reino Unido
Tipo de documento: Article
Volumen: 30 Número: 3
Páginas: 475-480
WOS Id: 000351660300022
ID de PubMed: 25348508

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